Biotech · Private company
Audentes Therapeutics
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Clinical trials30 recruiting or active
Pipeline programs1From trials and the company's site
Disclosed deals0None found yet
Cash runwayNot availablePrivate: no SEC financials
Pipeline1
- AT342Phase 1 · Crigler-Najjar SyndromeClinicalTrials.gov · fetched Nov 12, 2026
Clinical trials3
- AAV9 U7snRNA Gene Therapy to Treat Boys With DMD Exon 2 Duplications.PHASE1_PHASE2 · COMPLETED · started Jan 15, 2020ClinicalTrials.gov NCT04240314 · fetched Nov 12, 2026
- Gene Transfer Clinical Study in Crigler-Najjar SyndromePHASE1 · TERMINATED · started Sep 8, 2017ClinicalTrials.gov NCT03223194 · fetched Nov 12, 2026
- Clinical Assessment Study in Crigler-Najjar SyndromeCOMPLETED · started Mar 10, 2017ClinicalTrials.gov NCT03078881 · fetched Nov 12, 2026