Pharma · Public company · Novato, CA, US
Biomarin Pharmaceutical Inc
Ticker BMRN · SEC CIK 0001048477
Track this companyFree. Adds Biomarin Pharmaceutical Inc to your Dealase workspace and tells you when its record changes.
Clinical trials2525 recruiting or active
Pipeline programs16From trials and the company's site
Disclosed deals0None found yet
Cash runwayNot availableNo recent cash burn filed
Pipeline16
- BMN 111Phase 3 · AchondroplasiaClinicalTrials.gov · fetched Nov 12, 2026
- BMN 333Phase 3 · AchondroplasiaClinicalTrials.gov · fetched Nov 12, 2026
- Diet OnlyPhase 3 · Phenylketonuria (PKU)ClinicalTrials.gov · fetched Nov 12, 2026
- PegvaliasePhase 3 · Phenylketonuria (PKU)ClinicalTrials.gov · fetched Nov 12, 2026
- VosoritidePhase 3 · HypochondroplasiaClinicalTrials.gov · fetched Nov 12, 2026
- Vosoritide Injection [Voxzogo]Phase 3 · AchondroplasiaClinicalTrials.gov · fetched Nov 12, 2026
- Active BMN 111: Subcutaneous injection of recommended dose of BMN 111 based on weight-band dosing once daily.Phase 2 · AchondroplasiaClinicalTrials.gov · fetched Nov 12, 2026
- Human Growth HormonePhase 2 · Idiopathic Short StatureClinicalTrials.gov · fetched Nov 12, 2026
- Vosoritide InjectionPhase 2 · Noonan SyndromeClinicalTrials.gov · fetched Nov 12, 2026
- Vosoritide InjectionPhase 2 · Idiopathic Short StatureClinicalTrials.gov · fetched Nov 12, 2026
- BMN 349Phase 1 · Alpha 1-Antitrypsin DeficiencyClinicalTrials.gov · fetched Nov 12, 2026
- Administration KitLate-Infantile Neuronal Ceroid Lipofuscinosis Type 2ClinicalTrials.gov · fetched Nov 12, 2026
- Cerliponase AlfaLate-Infantile Neuronal Ceroid Lipofuscinosis Type 2ClinicalTrials.gov · fetched Nov 12, 2026
- MethotrexatePhenylketonuriaClinicalTrials.gov · fetched Nov 12, 2026
- PegvaliasePhenylketonuria, MaternalClinicalTrials.gov · fetched Nov 12, 2026
- PegvaliasePhenylketonuriaClinicalTrials.gov · fetched Nov 12, 2026
Clinical trials25
- Immune Modulation During Palynziq® Treatment in Adults (IMPALA)PHASE4 · RECRUITING · started May 29, 2026ClinicalTrials.gov NCT07477691 · fetched Nov 12, 2026
- Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With AchondroplasiaPHASE2_PHASE3 · RECRUITING · started Apr 20, 2026ClinicalTrials.gov NCT07441876 · fetched Nov 12, 2026
- A Study of Vosoritide Versus Placebo in Children With Hypochondroplasia Aged 0 to < 36 MonthsPHASE2 · RECRUITING · started Jul 30, 2025ClinicalTrials.gov NCT07126262 · fetched Nov 12, 2026
- Long-Term Extension Study of Vosoritide to Treat Children With HypochondroplasiaPHASE3 · ENROLLING_BY_INVITATION · started Jun 20, 2025ClinicalTrials.gov NCT07073014 · fetched Nov 12, 2026
- Study of BMN 349 Single Dose in PiZZ and PiMZ/MASH Adult ParticipantsPHASE1 · ACTIVE_NOT_RECRUITING · started Feb 21, 2025ClinicalTrials.gov NCT06738017 · fetched Nov 12, 2026
- A Study of Vosoritide in Children With Noonan Syndrome With Inadequate Growth During or After Human Growth Hormone TreatmentPHASE2 · ACTIVE_NOT_RECRUITING · started Nov 22, 2024ClinicalTrials.gov NCT06668805 · fetched Nov 12, 2026
- A Phase 2 Study of Vosoritide in Children With Idiopathic Short StaturePHASE2 · RECRUITING · started Oct 21, 2024ClinicalTrials.gov NCT06382155 · fetched Nov 12, 2026
- A Study to Assess Growth in Children With Idiopathic Short StatureRECRUITING · started Aug 8, 2024ClinicalTrials.gov NCT06309979 · fetched Nov 12, 2026
- Interventional Study of Vosoritide for the Treatment of Children With HypochondroplasiaPHASE3 · ACTIVE_NOT_RECRUITING · started Jun 17, 2024ClinicalTrials.gov NCT06455059 · fetched Nov 12, 2026
- A Long Term, Post-marketing Study of Immune Response in Patients Receiving Palynziq Treatment for PKU (PALisade)RECRUITING · started Jan 20, 2024ClinicalTrials.gov NCT06305234 · fetched Nov 12, 2026
- A Multicenter Multinational Observational Study of Children With HypochondroplasiaRECRUITING · started Nov 27, 2023ClinicalTrials.gov NCT06212947 · fetched Nov 12, 2026
- VIrtual STudy in Achondroplasia for the US (VISTA)RECRUITING · started Feb 21, 2023ClinicalTrials.gov NCT06168201 · fetched Nov 12, 2026
- A Long-Term Follow-Up Study in Severe Hemophilia A Subjects Who Received BMN 270 in a Prior BioMarin Clinical Trial (270-401)ENROLLING_BY_INVITATION · started Jan 1, 2023ClinicalTrials.gov NCT05768386 · fetched Nov 12, 2026
- A Global, Multicenter Study to Assess Maternal, Fetal and Infant Outcomes of Exposure to Palynziq® (Pegvaliase) During Pregnancy and BreastfeedingRECRUITING · started Nov 22, 2022ClinicalTrials.gov NCT05579548 · fetched Nov 12, 2026
- Study to Evaluate the Safety and Efficacy of Pegvaliase in Adolescents (Ages 12-17) With PhenylketonuriaPHASE3 · ACTIVE_NOT_RECRUITING · started Jun 17, 2022ClinicalTrials.gov NCT05270837 · fetched Nov 12, 2026
- A Long-term, Post-marketing Safety Study of Palynziq in Patients With PKU (PALace)RECRUITING · started Jun 6, 2022ClinicalTrials.gov NCT05813678 · fetched Nov 12, 2026
- The Effects of ATLAS Therapy on Nitric Oxide Bioavailability in Patients With Intermittent ClaudicationPHASE1 · ACTIVE_NOT_RECRUITING · started Jun 15, 2021ClinicalTrials.gov NCT04800692 · fetched Nov 12, 2026
- ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening ProgramENROLLING_BY_INVITATION · started May 10, 2021ClinicalTrials.gov NCT05368038 · fetched Nov 12, 2026
- Cerliponase Alfa Observational Study in the USACTIVE_NOT_RECRUITING · started Aug 19, 2020ClinicalTrials.gov NCT04476862 · fetched Nov 12, 2026
- Nutritional Impacts of Palynziq on Patients With Phenylketonuria (PKU)RECRUITING · started Oct 8, 2019ClinicalTrials.gov NCT04404530 · fetched Nov 12, 2026
- An Extension Study to Evaluate Safety and Efficacy of BMN 111 in Children With AchondroplasiaPHASE2 · ACTIVE_NOT_RECRUITING · started Jun 12, 2019ClinicalTrials.gov NCT03989947 · fetched Nov 12, 2026
- Examining Developmental Outcomes of Children Diagnosed With CLN2 DiseaseENROLLING_BY_INVITATION · started Dec 1, 2018ClinicalTrials.gov NCT03862274 · fetched Nov 12, 2026
- An Extension Study to Evaluate the Efficacy and Safety of BMN 111 in Children With AchondroplasiaPHASE3 · ACTIVE_NOT_RECRUITING · started Dec 12, 2017ClinicalTrials.gov NCT03424018 · fetched Nov 12, 2026
- Achondroplasia Natural History Multicenter Clinical StudyRECRUITING · started Apr 1, 2016ClinicalTrials.gov NCT02597881 · fetched Nov 12, 2026
- A Study to Evaluate Long-Term Safety, Tolerability, & Efficacy of BMN 111 in Children With Achondroplasia (ACH)PHASE2 · ACTIVE_NOT_RECRUITING · started Jan 26, 2016ClinicalTrials.gov NCT02724228 · fetched Nov 12, 2026
SEC filings12
- 10-Q · 10-QSEC EDGAR · filed Nov 3, 2026 · fetched Nov 12, 2026
- 8-K · 8-KSEC EDGAR · filed Nov 2, 2026 · fetched Nov 12, 2026
- 8-K · 8-KSEC EDGAR · filed Oct 6, 2026 · fetched Nov 12, 2026
- 8-K · 8-KSEC EDGAR · filed Sep 30, 2026 · fetched Nov 12, 2026
- 8-K · 8-KSEC EDGAR · filed Sep 15, 2026 · fetched Nov 12, 2026
- 8-K · 8-KSEC EDGAR · filed Sep 14, 2026 · fetched Nov 12, 2026
- 8-K · 8-KSEC EDGAR · filed Sep 1, 2026 · fetched Nov 12, 2026
- 8-K · 8-KSEC EDGAR · filed Aug 31, 2026 · fetched Nov 12, 2026
- 8-K · 8-KSEC EDGAR · filed Aug 18, 2026 · fetched Nov 12, 2026
- 10-Q · 10-QSEC EDGAR · filed Aug 6, 2026 · fetched Nov 12, 2026
- 8-K · 8-KSEC EDGAR · filed Aug 6, 2026 · fetched Nov 12, 2026
- 8-K/A · 8-K/ASEC EDGAR · filed Jul 13, 2026 · fetched Nov 12, 2026