Biotech · Private company
Neuren Pharmaceuticals Limited
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Clinical trials62 recruiting or active
Pipeline programs4From trials and the company's site
Disclosed deals0None found yet
Cash runwayNot availablePrivate: no SEC financials
Pipeline4
- NNZ-2591Phase 3 · Phelan-McDermid SyndromeClinicalTrials.gov · fetched Nov 12, 2026
- NNZ-2566Phase 2 · Rett SyndromeClinicalTrials.gov · fetched Nov 12, 2026
- NNZ-2591Phase 2 · Pitt Hopkins SyndromeClinicalTrials.gov · fetched Nov 12, 2026
- NNZ-2591Phase 2 · Prader-Willi SyndromeClinicalTrials.gov · fetched Nov 12, 2026
Clinical trials6
- An Open-label Study of NNZ-2591 in Pediatric Participants With Phelan-McDermid SyndromePHASE3 · RECRUITING · started Jun 8, 2026ClinicalTrials.gov NCT07593391 · fetched Nov 12, 2026
- A Study of NNZ-2591 in Pediatric Participants With Phelan-McDermid SyndromePHASE3 · RECRUITING · started Nov 12, 2025ClinicalTrials.gov NCT07281079 · fetched Nov 12, 2026
- An Open-Label Study of Oral NNZ-2591 in Prader-Willi Syndrome (PWS-001)PHASE2 · WITHDRAWN · started Sep 1, 2023ClinicalTrials.gov NCT05879614 · fetched Nov 12, 2026
- An Open-Label Study of Oral NNZ-2591 in Pitt Hopkins Syndrome (PTHS-001)PHASE2 · COMPLETED · started Oct 14, 2022ClinicalTrials.gov NCT05025332 · fetched Nov 12, 2026
- An Open-Label Study of Oral NNZ-2591 in Phelan-McDermid Syndrome (PMS-001)PHASE2 · COMPLETED · started Aug 8, 2022ClinicalTrials.gov NCT05025241 · fetched Nov 12, 2026
- A Safety Study of NNZ-2566 in Pediatric Rett SyndromePHASE2 · COMPLETED · started Mar 1, 2016ClinicalTrials.gov NCT02715115 · fetched Nov 12, 2026