Biotech · Private company
Orchard Therapeutics
Track this companyFree. Adds Orchard Therapeutics to your Dealase workspace and tells you when its record changes.
Clinical trials42 recruiting or active
Pipeline programs2From trials and the company's site
Disclosed deals0None found yet
Cash runwayNot availablePrivate: no SEC financials
Pipeline2
- Active Comparator: Allo-HSCTPhase 3 · MPS-IH (Hurler Syndrome)ClinicalTrials.gov · fetched Nov 12, 2026
- Experimental: OTL-203Phase 3 · MPS-IH (Hurler Syndrome)ClinicalTrials.gov · fetched Nov 12, 2026
Clinical trials4
- A Study to Investigate the Efficacy and Safety of OTL-203 in Subjects With MPS-IH Compared With Standard of Care With Allogeneic HSCTPHASE3 · ACTIVE_NOT_RECRUITING · started Dec 11, 2023ClinicalTrials.gov NCT06149403 · fetched Nov 12, 2026
- ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening ProgramENROLLING_BY_INVITATION · started May 10, 2021ClinicalTrials.gov NCT05368038 · fetched Nov 12, 2026
- Efficacy and Safety of the Cryopreserved Formulation of OTL-101 in Subjects With ADA-SCIDPHASE1_PHASE2 · COMPLETED · started Dec 16, 2016ClinicalTrials.gov NCT02999984 · fetched Nov 12, 2026
- Autologous CD34+ Hematopoietic Stem Cells Transduced ex Vivo With Elongation Factor 1 Alpha Shortened (EFS) Lentiviral Vector Encoding for the Human ADA GenePHASE1_PHASE2 · COMPLETED · started Aug 2, 2013ClinicalTrials.gov NCT01852071 · fetched Nov 12, 2026